Thrombotic microangiopathy following gene therapy for 5q-spinal muscular atrophy

by Biotech Newsroom


  • Lefebvre S, Burglen L, Reboullet S, Clermont O, Burlet P, Viollet L, et al. Identification and characterization of a spinal muscular atrophy-determining gene. Cell. 1995;80:155–65.

    Article 
    PubMed 
    CAS 

    Google Scholar
     

  • Finkel RS, McDermott MP, Kaufmann P, Darras BT, Chung WK, Sproule DM, et al. Observational study of spinal muscular atrophy type I and implications for clinical trials. Neurology. 2014;83:810–7.

    Article 
    PubMed 
    PubMed Central 

    Google…



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